Regenerative Medicine and the Promise of Stem Cell Research

Stem cells (SCs) have the ability to develop intodrugs.
many other types of cells. Totipotent cells knownTreatment of a child with leukemia would no
as blastomeres have the additional ability tolonger require a time-consuming and possibly
develop into an individual organism. Pluripotent cellsfruitless search for a bone marrow donor. Those
can develop into any kind of cell. Multipotent cellsrequiring a new kidney or new lung could provide
can develop into a variety of cells in a givenskin cells which would be directed to grow the
lineage such as connective tissue cells or epithelialneeded organ. Replacement parts would no longer
cells.be sought from parents, siblings, or first cousins.
Pluripotent cells include embryonic stem cells,Graft-versus-host disease, which has the potential
certain cells isolated from umbilical cord blood, andto kill the recipient, would be eliminated by using
adult stem cells which are found in bone marrow,the patient's own tissue to create the transplant.
the brain, and other locations. Overall, SCs may beSC research will also lead to new developments in
able to provide replacement tissue for treatmentgene therapy for conditions such as muscular
of many life-threatening diseases. Specialized cellsdystrophy and Huntington's disease. At present, a
and tissues derived from SCs may be used tosignificant roadblock to successful gene therapy is
treat Alzheimer's disease, Parkinson's disease,the mechanism of delivery of the replacement
stroke, Huntington's disease, amyotrophic lateralgenes. Early approaches packaged the
sclerosis (Lou Gehrig's disease), cancer, diabetes,replacement genes into viruses, using the viral
multiple sclerosis, muscular dystrophies, andparticles as the as the delivery vector. The field
rheumatoid arthritis.of gene therapy effectively came to a sudden
Also, research on SCs may lead to the ability tohalt in 1999 when a teenager died as a result of
grow organs such as the heart, kidney, liver, andbeing treated with such a viral vector. Insertion of
pancreas. These brand-new organs would be usedreplacement genes in stem cells derived from the
for transplantation, solving the ongoing severepatient will eliminate the possibility of such harms.
shortages of suitable available replacements.Successful treatment of chronic disease.
Ultimately it may be possible to grow organsSuccessful treatment of genetic disease. Slowing
from stem cells derived from a person's ownof the aging process. Organ transplantation.
somatic cells (such as a skin cell). A skin cell wouldImproved methods of treating severe injuries.
be reprogrammed to become an inducedStem cell research and the possibility of
pluripotent stem cell (iPS cell), and the iPS cellregenerative medicine are pointing the way
would be directed to become a kidney, liver, ortoward improved health and well-being for
whatever organ was needed. The astoundinghundreds of millions of people around the world.
benefit of being able to use iPS cells is that theMany practical roadblocks remain and there are
donor and the recipient are the same person. Themany grand challenges in this brand-new field. The
organ created is an automatic immunologic match,key is to make possible ongoing research.
thus avoiding the need for immunosuppressive